Denis, Alain; Mergaert, Lut; Fostier, Christel; … - In: Applied Health Economics and Health Policy 8 (2010) 5, pp. 343-350
implemented policies specifically designed to stimulate the development of orphan drugs. While decisions on orphan designation and … the marketing authorization of orphan drugs are made at the EU level, decisions on drug reimbursement are made at the … member state level. The specific features of orphan diseases and orphan drugs make them a high-priority issue for policy …